Therapeutics R&D Advanced cell / gene-based biopharmaceutical development and CDMO
What is Gene-Therapy ?
How Gene Therapy Works
Gene Therapy
Direct administration of therapeutic genes to the patient
Gene-Modified
Cell Therapy
Cells are extracted from the patient, genetically modified and then returned to the patient
Adeno-associated Virus (AAV)
What is adeno-associated virus (AAV)?
Technology to enhance the gene delivery efficiency of AAV vector
Advantages of AAV + Overcoming the low gene delivery efficiency